The Role of Precision Medicine and Emerging Genetic Therapies in the Japan Dravet Syndrome Sector for Late 2025
As we move through 2025, the scientific frontier in Japan is shifting from symptomatic relief toward disease-modifying therapies that target the root genetic cause of Dravet Syndrome. Investigational gene regulation therapies, such as antisense oligonucleotides (ASOs), are designed to upregulate the expression of the healthy SCN1A gene, potentially restoring the necessary levels of sodium...
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